Канал: CMT Research Foundation

Beyond The Diagnosis: Patient Stories, Expert Insights. Episode 1

Beyond The Diagnosis: Patient Stories, Expert Insights. Episode 1

CMT1A Clinical Trial and Drug Development Update

CMT1A Clinical Trial and Drug Development Update

Peter DeSilva - CMT Story

Peter DeSilva - CMT Story

CMT1A Research Update: Looking Towards Clinical Trials and Treatments

CMT1A Research Update: Looking Towards Clinical Trials and Treatments

The Greatest Gift: Bentzin $500,000 Match

The Greatest Gift: Bentzin $500,000 Match

The Greatest Gift: Eloise Schlafly

The Greatest Gift: Eloise Schlafly

The Greatest Gift: Tara Haik

The Greatest Gift: Tara Haik

The Greatest Gift: Bentzin $500,000 Match

The Greatest Gift: Bentzin $500,000 Match

The Greatest Gift: Michelle Moon

The Greatest Gift: Michelle Moon

The Greatest Gift: Lily Sander

The Greatest Gift: Lily Sander

The Bentzin Family: A $500,000 Match

The Bentzin Family: A $500,000 Match

Pushing Boundaries in CMT Research Early Stage Biotech Companies' Evolution and Insights on Therapy

Pushing Boundaries in CMT Research Early Stage Biotech Companies' Evolution and Insights on Therapy

Translating Academic Science to Business

Translating Academic Science to Business

Clinical Trial Readiness

Clinical Trial Readiness

The State of Gene Therapy in CMT

The State of Gene Therapy in CMT

Models of CMT

Models of CMT

Common Mechanisms of Disease

Common Mechanisms of Disease

Challenges in Drug Development

Challenges in Drug Development

Overview of the CMT Drug Development Pipeline

Overview of the CMT Drug Development Pipeline

Patient Fireside Chat - Life with CMT

Patient Fireside Chat - Life with CMT

Keynote Address

Keynote Address

Becoming Part of the Solution

Becoming Part of the Solution

Patient Powered Perspectives Biotech Insights on CMT and Collaborating with Patients

Patient Powered Perspectives Biotech Insights on CMT and Collaborating with Patients

Understanding the Importance of Genetic Testing

Understanding the Importance of Genetic Testing

Patient Voices

Patient Voices

2023 Kick Off Session

2023 Kick Off Session

CMT All Types

CMT All Types

Taking You Inside the Clinical Trial Process, Part I: The Scientific Perspective

Taking You Inside the Clinical Trial Process, Part I: The Scientific Perspective

Impacting Drug Development for CMT

Impacting Drug Development for CMT

Taking You Inside the Clinical Trial Process, Part II: The Patient Perspective

Taking You Inside the Clinical Trial Process, Part II: The Patient Perspective

2023 Convention Sizzle Reel

2023 Convention Sizzle Reel

Lucy and Chrysi - Fundraising for CMT

Lucy and Chrysi - Fundraising for CMT

A Conversation with Lily Sander

A Conversation with Lily Sander

Bracing and Orthotics: What You Need to Know

Bracing and Orthotics: What You Need to Know

Clinical Trial Readiness: What are Natural History Studies?

Clinical Trial Readiness: What are Natural History Studies?

Other Types/I Don't Know My Type

Other Types/I Don't Know My Type

Breakout Session: CMT 1A and 1B

Breakout Session: CMT 1A and 1B

2022 Global CMT Research Convention

2022 Global CMT Research Convention

2022 Global CMT Research Convention

2022 Global CMT Research Convention

Legacy- CMT Research Foundation Anthem

Legacy- CMT Research Foundation Anthem

Patients Changing the Pace of Clinical Trials - Dr. Don Wood, CEO of Muscular Dystrophy Association

Patients Changing the Pace of Clinical Trials - Dr. Don Wood, CEO of Muscular Dystrophy Association

An Overview of CMT1A - Dr. Bruce Carter, Vanderbilt University

An Overview of CMT1A - Dr. Bruce Carter, Vanderbilt University

Genetics of CMT: One Name, Many Diseases with Shawna Feely, University of Iowa

Genetics of CMT: One Name, Many Diseases with Shawna Feely, University of Iowa

Progress in Academic Basic in CMT Research - Dr. Rob Burgess, The Jackson Laboratory

Progress in Academic Basic in CMT Research - Dr. Rob Burgess, The Jackson Laboratory

Breakout session for other types of CMT – Dr. Brett McCray, Johns Hopkins University

Breakout session for other types of CMT – Dr. Brett McCray, Johns Hopkins University

Questions and Answers with Drs. Wood, Herrmann and Saporta

Questions and Answers with Drs. Wood, Herrmann and Saporta

Questions and Answers with Dr. Amanda Haidet-Philip , Dr. Sung-Chul and Dr. Keith Fargo

Questions and Answers with Dr. Amanda Haidet-Philip , Dr. Sung-Chul and Dr. Keith Fargo

Research Underway by Pharmaceutical Companies with Dr. Keith Fargo, CSO of the CMTRF

Research Underway by Pharmaceutical Companies with Dr. Keith Fargo, CSO of the CMTRF

The basic pathology of CMT with Dr. Keith Fargo, CSO of the CMT Research Foundation

The basic pathology of CMT with Dr. Keith Fargo, CSO of the CMT Research Foundation

CMT1A Endgame with CMT Research Foundation Board Member Peter deSilva

CMT1A Endgame with CMT Research Foundation Board Member Peter deSilva

Therapeutic Potential of CLZ-2002 by Remyelination and Nerve Regeneration - Dr. Sung-Chul Jung

Therapeutic Potential of CLZ-2002 by Remyelination and Nerve Regeneration - Dr. Sung-Chul Jung

Therapeutic Approaches Using Gene Therapy - Dr. Amanda Haidet-Philips

Therapeutic Approaches Using Gene Therapy - Dr. Amanda Haidet-Philips

Preparing for Clinical Trials in CMT - Dr. David Herrmann, University of Rochester

Preparing for Clinical Trials in CMT - Dr. David Herrmann, University of Rochester

Interventional Trials: Present and near Future - Dr. Mario Saporta, University of Miami

Interventional Trials: Present and near Future - Dr. Mario Saporta, University of Miami

Becoming Part of the Solution - The Graf Family

Becoming Part of the Solution - The Graf Family

Why we'll be there....

Why we'll be there....

Five reasons to attend the 2021 Global CMT Research Convention

Five reasons to attend the 2021 Global CMT Research Convention

Why I'll be there... Dr. Keith Fargo

Why I'll be there... Dr. Keith Fargo

Why I'll be there... Susan Ruediger

Why I'll be there... Susan Ruediger

Company Profile - Cellatoz

CMT Roundtable

CMT Roundtable

Conversations with CMT Experts : Demystifying the Drug Development Process

Conversations with CMT Experts : Demystifying the Drug Development Process

Conversations with CMT Experts: How We Change the Pace of Drug Development

Conversations with CMT Experts: How We Change the Pace of Drug Development

CMT and the FDA: Interview with Dr. Peter Marks

CMT and the FDA: Interview with Dr. Peter Marks

CMT 101: Therapy Development for CMT

CMT 101: Therapy Development for CMT

CMT 101: The Genetics of CMT

CMT 101: The Genetics of CMT

CMT 101: About CMT & the Peripheral Nervous System

CMT 101: About CMT & the Peripheral Nervous System

CMTRF 12 month Recap Webinar September 2019

CMTRF 12 month Recap Webinar September 2019