Канал: Center for Duchenne Muscular Dystrophy UCLA

CDMD 2021

CDMD 2021

Celebrating 10 Years of CDMD

Celebrating 10 Years of CDMD

Doubling Down on Duchenne 2018

Doubling Down on Duchenne 2018

ExonDys51 should be prescribed to DMD with amenable mutations.

ExonDys51 should be prescribed to DMD with amenable mutations.

Experts Support Exondys 51

Experts Support Exondys 51

CDMD Overview

CDMD Overview

ADCOM Response - Eteplirsen Approved!

ADCOM Response - Eteplirsen Approved!

FDA decision on eteplirsen delayed

FDA decision on eteplirsen delayed

AdCom Overall

AdCom Overall

Abbreviated Response to the April 25th Advisory Committee

Abbreviated Response to the April 25th Advisory Committee

Our response to the April 25th Advisory Committee

Our response to the April 25th Advisory Committee

An emotional day.

An emotional day.

An update during lunch? - April 25 FDA AdCom

An update during lunch? - April 25 FDA AdCom

April 25 - Day of FDA Advisory Committee Meeting

April 25 - Day of FDA Advisory Committee Meeting

Where we are so far!

Where we are so far!

April 24 - The day before FDA Advisory Committee Meeting

April 24 - The day before FDA Advisory Committee Meeting

Leading Up to AdCom

Leading Up to AdCom

What is an AdCom?

What is an AdCom?

Why Is there an AdCom for Eteplirsen.

Why Is there an AdCom for Eteplirsen.

Treatment of Duchenne So Far

Treatment of Duchenne So Far

Why Approve Eteplirsen?

Why Approve Eteplirsen?

"An End to Duchenne: Gene Editing for Muscular Dystrophy" - Courtney Young

"An End to Duchenne: Gene Editing for Muscular Dystrophy" - Courtney Young

J.J. Abrams Supports Duchenne Research

J.J. Abrams Supports Duchenne Research

Dylan's SMOSH video gets over 1 Million views!

Dylan's SMOSH video gets over 1 Million views!

300,000 Views

300,000 Views

Co-Director Stanley Nelson BE REASONABLE

Co-Director Stanley Nelson BE REASONABLE

Matt McCoy BE REASONABLE

Matt McCoy BE REASONABLE

Joel Murray BE REASONABLE

Joel Murray BE REASONABLE

Melissa Spencer BE REASONABLE

Melissa Spencer BE REASONABLE

Jenno Topping and Chris Moore BE REASONABLE

Jenno Topping and Chris Moore BE REASONABLE

Co-Director Carrie Meceli BE REASONABLE

Co-Director Carrie Meceli BE REASONABLE

Dylan Improv 2015

Dylan Improv 2015

Be Reasonable Accelerated Approval For Duchenne

Be Reasonable Accelerated Approval For Duchenne

Be Reasonable video

Be Reasonable video

Rachel Crosbie-Watson on the Muscle Cell Biology Training Program

Rachel Crosbie-Watson on the Muscle Cell Biology Training Program

Dealing For Duchenne 2014

Dealing For Duchenne 2014

The Center for Duchenne Muscular Dystrophy at UCLA 2015

The Center for Duchenne Muscular Dystrophy at UCLA 2015

Be Reasonable - Accelerated Approvals For Duchenne

Be Reasonable - Accelerated Approvals For Duchenne