Checkorphan

CheckOrphan: The Longest Running Website Focused Exclusively on Rare Diseases

The Orphan Drug Act and Rare Disease Drug Pricing

Dup15q Syndrome Research

Dup15q Syndrome Overview

Emerging Treatment Options for Patients Suffering from X-Linked Retinoschisis

Alnylam Pharma and the Science of RNAi

The Importance of Advocacy Groups for Rare Disease Patients

Challenges of Diagnosing Patients for PAP and Lung Infection in Cystic Fibrosis

Robert Derham: Patent Exclusivity and the Orphan Drug Act

PellePharm and it's Lead Drug Candidate Patidegib

Challenges of Recruiting Patients for Rare Disease Clinical Trials

Still's Disease Clinical Trial

Potential Market for Actinium's Iomab-B

Patients as the Center of the Drug Development Process

Onxeo's Orphan Oncology Pipeline

The Patients' Journey Toward a Diagnosis of Myeloproliferative Neoplasms (MPNs)

22q11.2 Deletion Syndrome

How the Children's Tumor Foundation Works With Industry

Myths Surrounding the Orphan Drug Act

PellePharm's CEO Discusses the Importance of Advocacy Groups to Their Company