Pediatric neurologist Dr. Crystal Proud discusses the recent advancements in gene therapy and gene transfer technology as it relates to Duchenne Muscular Dystrophy (DMD). Learn about the evolution of data available from clinical trials, and discover the opportunities for improving patient outcomes.
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This education is brought to you by the France Foundation and supported by an educational grant from Sarepta Therapeutics Inc. All information is intended for healthcare professionals.
DMD Gene Therapy Clinical Trials
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DMDICNMDDuchenneMuscular DystrophyServaisNeuromuscularGeneticDystrophingene therapyphenotypesneuromuscular disordersDuchenne Muscular Dystrophyanti-inflammatorygene mutationsnovel therapieshealthcarediseaserare diseasechronic weaknesschronic illnessclinical trialsminidystrophinmicrodystrophingenetic disorderstransgeneanti-transgeneShiehnewborn screeningRUSPWMSBiomarkersimmune response