#TOP10
#ZOLGENSMA
#ACTIMMUNE
ZOLGENSMA
onasemnogene abeparvovec
Indication
Spinal Muscular atrophy ( deterioration in motor neuron )
USFDA approval 2019
Developed by : AVEXIS
Manufactured by : NOVARTIS
ACTIMMUNE
Interferon gamma -16
Manufactured by : Horizone Therapeutics
Indication
SMO Severe malignant osteopetrosis
CGD Chronic granulomatous disease
ACTHAR
Repository corticopin injection
Manufactured by
Mallinkrodt pharmacuetical
Indication
Rheumatoid arthritis
Multiple sclerosis
Psoriatic arthritis
Infantile spasm or seizure
Acortan Acthar Acton Cortigel Trofocortina .
Myalept Amryt Pharma
Ravicti Horizon Therapeutics
Mavenclad EMD Serono, Inc
Actimmune Horizon Therapeutics
Oxervate Dompé
Takhzyro Takeda
Daraprim Vyera Pharmaceuticals
Juxtapid Amryt Pharma
Cinryze Takeda
Chenodal Retrophin, Inc
Gattex Takeda
H.P. Acthar Mallinckrodt Pharmaceuticals
Tegsedi Akcea Therapeutics
Vitrakvi Bayer Pharmaceuticals
Ayvakit Blueprint Medicines
Kynamro Kastle Therapeutics
Sovaldi Gilead
Viekira Pak Abbvie
Viekira XR Abbvie
Tibsovo Agios Pharmaceuticals
Most expensive FDA approved drug
the most expensive drug in the US?
Why is Zolgensma so expensive?
Most expensive medical treatment
Expensive drugs for rare diseases
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