To read more about this clinical trial, please visit [ Ссылка ]

Cleveland Clinic researchers are taking part in a clinical trial evaluating the safety and effectiveness of a gene therapy to treat sickle cell disease.

Rabi Hanna, MD, director of the pediatric blood and bone marrow transplant program at Cleveland Clinic Children's, gives an update on the RUBY trial to assess a single dose of EDIT-301. The gene editing cell therapy modifies a patient's own stem cells to correct the mutation responsible for sickle cell disease.

For more information about sickle cell disease, please visit [ Ссылка ]

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