Gina Ruiz, an adult with cystic fibrosis, is not eligible for existing CFTR modulators because of her nonsense mutations. This experience has felt isolating and lonely, and like she can't relate to others in the CF community. However, Gina still remains hopeful about the potential of genetic therapies.
This video was featured in Plenary 1 of the 2023 North American Cystic Fibrosis Conference.
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