A 5-minute video explanation by Phelan-McDermid Syndrome Foundation (PMSF) Scientific Director, Dr. Kate Still. Antisense oligonucleotides are an up-and-coming technology which may apply to Phelan-McDermid syndrome. But what are they and why are we hearing more about them? How do they differ from other techniques? What are the challenges? What is the timeline? What is the hope?
Find the closed caption text here: [ Ссылка ]
ASO blog post: [ Ссылка ]
Learn more about Phelan-McDermid syndrome here: [ Ссылка ]
